De Luca, Michele, and Giulio Cossu. "Cost and Availability of Novel Cell and Gene Therapies." EMBO Reports 24, no. 2 (2023): e56661. https://doi.org/10.15252/embr.202256661
Abstract:
Advanced gene and cellular therapies risk a second “valley of death” due to their high costs and low patient population. As these are life-saving therapies, measures are urgently needed to prevent their withdrawal from the market.