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Why are animal models used when testing the safety of a new therapy?
What role do preclinical and clinical trials play in ensuring patient safety?
Why are some conditions more suitable for gene and cell therapies than others?
There is an approved treatment available for my condition - why can't I receive it?
How to look for approved medicines?
How are medicines developed and approved?

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Glossary

Accelerated assessment
Adeno-associated virus (AAV)
Adenovirus
Adult stem cells
Advanced Therapy Investigational Medicinal Product (ATIMP)
Advanced Therapy Medicinal Product (ATMP)
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Current and Potential Uses

Resources & Factsheets

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What is CAR T-cell therapy?

Related Topics Blood disorders Cancer Blood Stem Cells CAR-T Therapy Current and Potential Uses Reprogramming
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International Guidelines for the Treatment of Huntington's Disease

Related Topics Huntington's Disease Neurological Disorders Current and Potential Uses Ethics and Society
EuroGCT Resource

Where should I start?

Related Topics Cell and Gene Fundamentals Cell Therapy Clinical Trials Current and Potential Uses Ethics and Society Gene Therapy Methods and Tools Patient Involvement Policy & Regulation Research
EuroGCT Resource

There is an approved treatment available for my condition - why can't I receive it?

Related Topics Rare Diseases Clinical Trials Current and Potential Uses Ethics and Society Industry Policy & Regulation Unproven Treatments

Report: ATMPs and equity of access

Related Topics Rare Diseases Current and Potential Uses
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Taking part in clinical trials: MRI scans

Related Topics Parkinson's Disease Clinical Trials Current and Potential Uses Patient Involvement Unproven Treatments
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Taking part in clinical trials: MRI and PET

Related Topics Neurological Disorders Parkinson's Disease Clinical Trials Current and Potential Uses Patient Involvement Unproven Treatments
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The value of Patient and Public Involvement: Interviews with PPI contributors

Related Topics Huntington's Disease Neurological Disorders Parkinson's Disease Cell Therapy Current and Potential Uses Patient Involvement Unproven Treatments
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LEARN Study: A checklist for people with Parkinson's Disease considering study participation

Related Topics Neurological Disorders Parkinson's Disease Cell Therapy Clinical Trials Current and Potential Uses Patient Involvement Unproven Treatments
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LEARN Study: Summary of outcomes

Related Topics Huntington's Disease Parkinson's Disease Cell Therapy Current and Potential Uses Patient Involvement
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