Clinical Trials and Patient Involvement

Patient voices are essential for the development of new therapies. The clinical trials process, an essential step in establishing the safety and efficacy of a therapy, relies on the generous involvement of patient participants. The therapy development process also benefits from the guidance and insight of people directly affected by genetic conditions, as they are experts in their own needs and experiences. This section provides information about the different pathways through which patients and members of the public can contribute to gene and cell therapy.