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FAQs

Why are animal models used when testing the safety of a new therapy?
What role do preclinical and clinical trials play in ensuring patient safety?
Why are some conditions more suitable for gene and cell therapies than others?
There is an approved treatment available for my condition - why can't I receive it?
How to look for approved medicines?
How are medicines developed and approved?

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Glossary

Accelerated assessment
Adeno-associated virus (AAV)
Adenovirus
Adult stem cells
Advanced Therapy Investigational Medicinal Product (ATIMP)
Advanced Therapy Medicinal Product (ATMP)
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Factsheets

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Condition
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Illustration of a neuron affected by Alzheimer's Disease

Alzheimer's Disease - how could gene and cell therapy help?

Related Topics Alzheimer's Disease Neurological Disorders Factsheets
English
EuroGCT Resource

Inherited retinal disorders (IRD): how could gene and cell therapy help?

Related Topics Eye Disease Current and Potential Uses Factsheets
English
EuroGCT Resource
Limbal stem cells in the human cornea

Eye disease: how could gene and cell therapy help?

Related Topics Eye Disease Factsheets
English
EuroGCT Resource
credit: Professor Benjamin Beck

Cancer: a disease of stem cells?

Related Topics Cancer Cell Therapy Factsheets iPS cells
English
EuroGCT Resource
Fluorescence microscopy image of an oligodendrocyte

Multiple sclerosis: how could gene and cell therapy help?

Related Topics Multiple Sclerosis Neurological Disorders Blood Stem Cells Cell Therapy Factsheets
English
EuroGCT Resource
Laboratory-grown nerve cells, shown with fluorescent green dye against a black background

Parkinson's Disease: How could gene and cell therapy help?

Related Topics Neurological Disorders Parkinson's Disease Cell Therapy Clinical Trials Current and Potential Uses Factsheets Gene Therapy iPS cells Reprogramming
English
Image of intestinal epithelial cells

Short bowel syndrome: how can gene and cell therapy help?

Related Topics Bowel Disease Current and Potential Uses Disease Modelling Factsheets iPS cells Tissue Engineering
English
EuroGCT Resource
Photograph of a healthy liver

Chronic liver disease: how could gene and cell therapy help?

Related Topics Liver Disease Cell Therapy Current and Potential Uses Factsheets iPS cells Organoids Tissue Engineering
DNA teaser image

What is the clinical trials process?

Related Topics Clinical Trials Factsheets Patient Involvement Policy & Regulation Research Unproven Treatments
EuroGCT Resource
DNA teaser

What are 'unproven' therapies?

Related Topics Clinical Trials Current and Potential Uses Ethics and Society Factsheets MSCs Policy & Regulation Unproven Treatments
EuroGCT Resource
DNA teaser image

CAR-T Therapy

Related Topics Blood disorders Cancer Immune Conditions Rare Diseases Blood Stem Cells CAR-T Therapy Cell Therapy Clinical Trials Current and Potential Uses Factsheets Gene Editing Gene Therapy
EuroGCT Resource
Child with EB in the clinic

Epidermolysis Bullosa: How could gene and cell therapy help?

Related Topics Epidermolysis Bullosa Rare Diseases Skin Factsheets
EuroGCT Resource
Current and Potential Uses Generic Logo

What conditions can currently be treated using gene and cell therapy?

Related Topics Blood disorders Cancer Eye Disease Immune Conditions Multiple Sclerosis Rare Diseases Blood Stem Cells CAR-T Therapy Cell Therapy Current and Potential Uses Explore Stem Cells Factsheets Gene Editing Gene Therapy
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Reproduction and fertility : how could gene and cell therapy help?

Related Topics Reproduction and Fertility iPS cells
EuroGCT Resource
Diagram of the spinal cord

Spinal cord injuries - how could gene and cell therapies help?

Related Topics Spinal Cord Injuries Factsheets
English

Age-related macular degeneration: how could gene and cell therapy help?

Related Topics Eye Disease Current and Potential Uses Factsheets
English
EuroGCT Resource
Image of neurons grown from embryonic stem cells in the lab

Stroke: how could gene and cell therapy help?

Related Topics Neurological Disorders Stroke Factsheets
English
EuroGCT Resource
Fluorescence microscopy image of embryonic stem cells

Embryonic stem cells: where do they come from and what can they do?

Related Topics Embryonic Stem Cells Explore Stem Cells Factsheets
English
EuroGCT Resource
Diagram showing stem cell differentiation and renewal

Types of stem cells and their uses

Related Topics Blood Stem Cells Cell and Gene Fundamentals Embryonic Stem Cells Explore Stem Cells Factsheets iPS cells MSCs Skin Stem Cells
English
EuroGCT Resource
Microscopy image of iPS cells

Using 'reprogrammed' cells to model diseases

Related Topics Disease Modelling iPS cells
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